A single injection into the inner ear restored functional hearing in 90% of people born deaf because of mutations in the OTOF ...

First FDA-approved gene therapy for hearing loss targets a rare inherited form of deafness Treatment restored hearing in most ...

A method has been developed for patients with congenital hearing impairment, who previously needed medical devices like ...

SEATTLE — Some of our most challenging health conditions result from genetic disorders like sickle cell disease and certain cancers. Gene therapy is revolutionizing how they're treated, and the Fred ...

The US Food and Drug Administration (FDA) has released draft guidance on how sponsors can utilize next-generation sequencing ...

Scientists looked at multiple techniques used to measure the modified viruses deployed in some gene therapy research and treatments. One technique, known as SEC-MALS, was the most precise and accurate ...

The special properties of methylcellulose foam could make it a vehicle for bedside genetic engineering, according to a proof-of-principle study from bioengineers at Fred Hutch Cancer Center. In the ...

Cell and gene therapies are moving towards correcting root causes of diseases. Let's take a look at future cell and gene therapy trends.

The Breakthrough Prize Foundation awarded researchers involved in developing gene therapies for blindness and sickle cell ...

The global gene therapy market size is projected to expand significantly, with an estimated value of USD 19.3 billion by 2034 ...

Most gene-editing tools cut DNA wherever they’re pointed, with no way to tell a tumor cell from a healthy one. A study ...

Some gene therapy treatments use modified adeno-associated viruses (AAVs) like the one shown here to deliver therapeutic genetic material into a patient’s cells. In a finding with implications for one ...