How Gene Therapy Works

New Gene Therapy Can Restore Hearing in Deaf Kids

New Gene Therapy Can Restore Hearing in Deaf Kids—And It Comes With an Unexpected Price Tag

A first-of-its-kind gene therapy that can restore hearing in children born deaf has just cleared its final hurdle—and, in a rare move, it will be free. On Thursday, the U.S. Food and Drug Administration approved Otarmeni,

Harvard Medical School · 1d

Hearing Restoration From Gene Therapy for Inherited Deafness Lasts Years, New Trial Results Show

· 1d

'A landmark moment for the field': FDA approves first-ever gene therapy for inherited deafness

Rolling Out

Why gene therapy could revolutionize how we treat disease

Gene therapy represents one of medicine’s most ambitious attempts to treat disease at its root cause by altering the genetic code itself. The approach works by recovering the functions of ...

Penn Medicine, Children's Hospital of Philadelphia team awarded Breakthrough Prize for developing gene therapy for inherited blindness

LOS ANGELES, April 18, 2026 /PRNewswire/ -- Their discovery started with a group of blind dogs living at a vet school. Now, the work has been awarded the prestigious Breakthrough Prize at the "Oscars ...

OCGN's Gene-Agnostic Strategy Could Reset Retinal Therapy

Ocugen's gene-agnostic therapy strategy targets broad retinal patient groups with one-time treatments, setting up major 2026-27 catalyst events.

Some results have been hidden because they may be inaccessible to you

Show inaccessible results