NEW YORK and CLEVELAND, Feb. 12, 2020 (GLOBE NEWSWIRE) -- Abeona Therapeutics Inc. (Nasdaq: ABEO), a fully-integrated leader in gene and cell therapy, today announced that researchers from the Abigail ...

Ultragenyx Pharmaceuticals RARE announced that the FDA has issued a Complete Response Letter (CRL) for its biologics license application (BLA) for UX111. The AAV gene therapy is being developed as a ...

Neurocognitive development of youngest patients preserved 12-18 months post treatment; development scores remain within range of unaffected children Robust and sustained biomarker improvement across ...

MPS Art Therapy recently caught up with first-year MPS Art Therapy student Nicole Titus, who provided insight on what led her to SVA in pursuit of a career in Art Therapy. What inspired you to pursue ...

Orchard Therapeutics has signed an exclusive global license with Fondazione Telethon and Ospedale San Raffaele in Milan, Italy, for what will be the company’s sixth clinical stage ex vivo autologous ...

Researchers are closer to finding a better way to treat children with a rare metabolic disorder called MPS I. It is caused by a deficiency of the key enzyme IDUA needed to break down complex sugars in ...

Through the end of June, visitors are encouraged to view and interact with the artwork on display in the MPS Art Therapy gallery space for "In My Truth, In My Power," an exhibition presenting work by ...

(MENAFN- EIN Presswire) EINPresswire / -- The National MPS Society announced a landmark $4 million donor-directed grant to support a pioneering gene therapy program for MPS IIIB (Sanfilippo syndrome ...

Pain relief for chronic pain sufferers may often seem like the pot of gold at the end of an ever-receding rainbow. So many therapies promise relief but don't end up delivering, leaving pain sufferers ...

In the Spring/Summer 2018 issue, Prattfolio asked leaders from the Pratt alumni community to share their wisdom from the helm—how they inspire, improve, and ignite creativity. This is part one in a ...