Pick's disease, more commonly known today as frontotemporal dementia (FTD), is a neurodegenerative disease that causes the progressive deterioration of the two largest lobes of the brain.

Monarez is the CDC's acting director and a longtime biosecurity expert with ties to former President Biden’s flagship health ...

In the space of four days, the number of FDA-approved therapies for ultra-rare genetic disorder Niemann-Pick disease has gone from zero to two, transforming the prospects for patients. IntraBio's ...

FDA approval of Miplyffa last September made the Zevra drug the first treatment for Niemann Pick disease type C (NPC), an inherited disorder that leads to defective enzymes important in cellular ...

A new study in the peer-reviewed journal Human Gene Therapy showed that more than half of individuals with Niemann-Pick disease, type C1 (NPC1) who were tested lacked neutralizing antibodies against ...