Victoria Gray, the first person cured of sickle cell using CRISPR gene editing therapies, spoke in Fargo about her journey and the need to lower the $2M treatment cost.

For decades, scientists have studied how to control DNA—the molecule that holds the instructions for all life. One of the ...

Mitochondria supply the body with the energy currency adenosine triphosphate (ATP), which drives all bodily activities. For ...

Germany, have developed a new method to better understand the energy production of human cells. Defects in this process lead to serious and often fatal disorders that can affect skeletal muscle and ...

Scribe Therapeutics Inc. (Scribe), a genetic medicines company unlocking the potential of CRISPR to transform human health, presented data on two therapeutic applications of its genome editing and ...

The researchers used the gene scissors CRISPR/Cas9 to introduce various ALS-causing mutations into human ... in the cells and their communication and necessary contacts with muscle fibers.

In a world first, a baby in the U.S. received a personalized, CRISPR-based gene therapy that corrects a specific ... The results were also presented at the American Society of Gene & Cell Therapy's ...

Modeling cardiovascular diseases using CRISPR-Cas9 genome editing in induced pluripotent stem cells (iPSCs ... ensure Cas9 expression specifically in the heart and muscle. sgRNAs are packaged into a ...

In addition to the conferred standardization, the availability of such cell lines opened avenues for the design of tailored eECMs by applying dedicated genetic tools. In this study, we demonstrated ...

The condition causes the heart muscle to ... in which some cells have the unwanted mutations and others don’t. So the team developed a new method: injecting sperm and CRISPR into the egg ...

This valuable study provides solid support for the participation of the BMP-binding domain of MuSK, a tyrosine kinase mostly known for its role at the neuromuscular junction, in the maintenance and ...