Though it may be a while before similar personalized treatments are available for others, doctors hope the technology can ...

An infant with a rare urea cycle disorder became the first patient to receive a personalized gene-editing therapy. His care ...

Another Breakthrough Summit West in the books, and what an excellent event! We kicked off the day with former FDA head Robert ...

The goal is to reuse key parts of the treatment and simply swap in a custom set of instructions for each patient's specific gene mutation, doctors say.