A Wigan family has teamed up with a national charity to help raise awareness of a rare genetic disease which affects both a ...

Though it may be a while before similar personalized treatments are available for others, doctors hope the technology can ...

An infant with a rare urea cycle disorder became the first patient to receive a personalized gene-editing therapy. His care ...

Another Breakthrough Summit West in the books, and what an excellent event! We kicked off the day with former FDA head Robert ...

The goal is to reuse key parts of the treatment and simply swap in a custom set of instructions for each patient's specific gene mutation, doctors say.

KJ Muldoon was born with a devastating medical problem. Racing to solve it, doctors may have launched a 'road map' for a new type of treatment.

For the first time, doctors have created a customized treatment using the revolutionary gene-editing technique known as ...

Though it may be a while before similar personalized treatments are available for others, doctors hope the technology can ...

Scientists sprinted to create personalized medicine for baby KJ powered by CRISPR, a powerful gene-editing technology that ...

In a Brazilian village, a rare disease has affected many children. Research links it to cousin marriages, revealing how ...