14 Nov – Fred Cheng recently celebrated turning 41 by revealing that his focus this year has been on son Asher.
Joseph Schwartz has given his Buy rating due to a combination of factors surrounding Ultragenyx Pharmaceutical’s GTX-102 program for Angelman syndrome. The updated data from the Phase 1/2 trial, ...
Ultragenyx Pharmaceutical Inc. (RARE) announced Phase 1/2 data in support of the Phase 3 Aspire study for GTX-102, its ...
A four-year-old girl with DUP15q syndrome, who doctors said would never walk, has defied expectations to take her first steps.