Mitochondria supply the body with the energy currency adenosine triphosphate (ATP), which drives all bodily activities. For ...

A new technique that alters protein production in mitochondria could help researchers understand mitochondrial diseases as ...

The researchers used the gene scissors CRISPR/Cas9 to introduce various ALS-causing mutations into human ... in the cells and their communication and necessary contacts with muscle fibers.

Germany, have developed a new method to better understand the energy production of human cells. Defects in this process lead to serious and often fatal disorders that can affect skeletal muscle and ...

Prime editing is an advanced gene editing technology that enables precise DNA corrections without introducing double-stranded ...

Since the approval of Luxturna, there has been a wave of gene therapies advancing in clinical trials to treat genetic vision ...

In axolotls, retinoic acid acts like a molecular GPS. Its concentration changes along the length of a regenerating limb, ...

Using a simple zebrafish model of the ultra-rare genetic disease XMEA, researchers were able to test 30 clinically tested ...

XMEA is a recessive, genetic disease that causes progressive muscle weakness. Can a small fish help identify possible ...

Can a small fish help identify possible treatments for an ultra-rare inherited disease found in an Alabama boy? The genetic ...

DataM Intelligence | competitive Intelligence Gene therapies, exon-skipping drugs and next-gen steroids are reshaping Duchenne muscular dys ...