Mayo Clinic's Engineering & Therapeutics in Gastrointestinal Disease Lab is developing new ways to deliver gene therapy into organs through endoscopic procedures endoscopists already perform.

Gene editing has emerged as a powerful approach for targeting the genetic causes of disease, but getting the editing ...

Russia's Minister of Science and Education, Denis Sekirinsky, has claimed that researchers in his country are on track to ...

Russian scientists are reportedly developing a world-first gene therapy targeting the RAGE receptor to halt cellular aging.

A first-of-its-kind gene therapy that can restore hearing in children born deaf has just cleared its final hurdle—and, in a ...

Myofibrillar myopathy type 6 (MFM6) is a rare genetic muscle disorder that leads to severe muscle weakness and a drastically ...

Regeneron will make its newly approved gene therapy available for free in the U.S. The company hasn't yet decided how much it ...

Providers and payers certainly face some formidable challenges when it comes to gene therapy, but it pales in comparison to ...

The FDA is signaling change, but actual success depends on more than simply bringing in a new leader at the Center for ...

The U.S. Food and Drug Administration (FDA) has approved the first-ever gene therapy for inherited deafness.

Trump’s new big pharma deal announced today aims to lower drug prices nationwide, expand Medicaid savings, and cut costs for ...