Scientists at UCLA have created one of the first cellular-resolution molecular maps detailing how Down syndrome alters human ...
CAR T cell therapy wipes out rogue antibodies' source and improves walking speed in people with the same autoimmune disorder ...
A doctor reflects on how raising a son with Angelman syndrome reshaped his family, deepened his empathy and turned grief into ...
The blood-brain border has long stymied drug development for neurodegenerative diseases. In recent years, Denali, Roche, and others have designed molecular brain shuttles that ferry investigational ...
A collaborative research study co-led by scientists at the Icahn School of Medicine at Mount Sinai and the Liber Institute for Brain Development has for the first time identified a biological process ...
A collaborative research study co-led by scientists at the Icahn School of Medicine at Mount Sinai and the Liber Institute for Brain Development has for the first time identified a biological process ...
Denali Therapeutics’ tividenofusp alfa (Avlayah) has secured accelerated approval for Hunter syndrome, a rare metabolic disease. The first-in-modality biologic — an enzyme fused to a blood–brain ...
Hunter syndrome patients can manage the disorder with a drug that addresses disease symptoms throughout the body except the brain — a key limitation for treating this rare neurological disorder. The ...
Strongest El Niño in a century? What this rare phenomenon could bring. 'Very dangerous': Ex-general sounds alarm after Hegseth fires officers Trump administration finalizes better-than-feared Medicare ...
Katie has a PhD in maths, specializing in the intersection of dynamical systems and number theory. She reports on topics from maths and history to society and animals. Katie has a PhD in maths, ...